Display options
Share it on

Hum Gene Ther. 2021 Oct;32(19):1270-1279. doi: 10.1089/hum.2020.318. Epub 2021 May 06.

Optimized Protocol for Accurate Titration of Adeno-Associated Virus Vectors.

Human gene therapy

Tuisku Suoranta, Nihay Laham-Karam, Seppo Ylä-Herttuala

Affiliations

  1. A. I. Virtanen Institute for Molecular Sciences, University of Eastern Finland, Kuopio, Finland.
  2. Heart Center, Kuopio University Hospital, Kuopio, Finland.
  3. Gene Therapy Unit, Kuopio University Hospital, Kuopio, Finland.

PMID: 33560161 DOI: 10.1089/hum.2020.318

Abstract

Adeno-associated virus (AAV) is currently the most popular gene delivery vector for

Keywords: AAV; AAV titration; adeno-associated virus; ddPCR; gene therapy; genome extraction; qPCR

Publication Types