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Ozes B, Moss K, Myers M, et al. AAV1.NT-3 gene therapy in a CMT2D model: phenotypic improvements in . Brain Commun. 2021;3(4):fcab252doi: 10.1093/braincomms/fcab252.
Ozes, B., Moss, K., Myers, M., Ridgley, A., Chen, L., Murrey, D., & Sahenk, Z. (2021). AAV1.NT-3 gene therapy in a CMT2D model: phenotypic improvements in . Brain communications, 3(4), fcab252. https://doi.org/10.1093/braincomms/fcab252
Ozes, Burcak, et al. "AAV1.NT-3 gene therapy in a CMT2D model: phenotypic improvements in ." Brain communications vol. 3,4 (2021): fcab252. doi: https://doi.org/10.1093/braincomms/fcab252
Ozes B, Moss K, Myers M, Ridgley A, Chen L, Murrey D, Sahenk Z. AAV1.NT-3 gene therapy in a CMT2D model: phenotypic improvements in . Brain Commun. 2021 Oct 23;3(4):fcab252. doi: 10.1093/braincomms/fcab252. eCollection 2021. PMID: 34755111; PMCID: PMC8568849.
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Brain Commun. 2021 Oct 23;3(4):fcab252. doi: 10.1093/braincomms/fcab252. eCollection 2021.

AAV1.NT-3 gene therapy in a CMT2D model: phenotypic improvements in .

Brain communications

Burcak Ozes, Kyle Moss, Morgan Myers, Alicia Ridgley, Lei Chen, Darren Murrey, Zarife Sahenk

Affiliations

  1. Department of Pediatrics, Center for Gene Therapy, The Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH 43205, USA.
  2. Department of Pediatrics and Neurology, Nationwide Children's Hospital and The Ohio State University, Columbus, OH 43205, USA.
  3. Department of Pathology and Laboratory Medicine, Nationwide Children's Hospital, Columbus, OH 43205, USA.

PMID: 34755111 PMCID: PMC8568849 DOI: 10.1093/braincomms/fcab252

Abstract

Glycyl-tRNA synthetase mutations are associated to the Charcot-Marie-Tooth disease type-2D. The

© The Author(s) (2021). Published by Oxford University Press on behalf of the Guarantors of Brain.

Keywords: AAV; CMT2D; NT-3; gars

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