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J Genet Syndr Gene Ther. 2011 Nov 16;1(3). doi: 10.4172/2157-7412.S1-003.

Engineered Hematopoietic Stem Cells as Therapeutics for Hemophilia A.

Journal of genetic syndromes & gene therapy

Philip M Zakas, H Trent Spencer, Christopher B Doering

Affiliations

  1. Graduate Program in Molecular and Systems Pharmacology, Graduate Division of Biological and Biomedical Sciences, Emory University.
  2. Aflac Cancer Center and Blood Disorders Service, Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia.

PMID: 25383239 PMCID: PMC4220243 DOI: 10.4172/2157-7412.S1-003

[No abstract available.]

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