Gene Therapy: It Is Time to Talk about High-Dose AAV: The deaths of two children with X-linked myotubular myopathy in the ASPIRO trial prompts a reexamination of …. Paulk N. N Paulk - Genetic Engineering & Biotechnology News, 2020 - liebertpub.com GSID: Cqr9zUYgkTEJ
Fourth Boy Dies in Clinical Trial of Astellas' AT132. [No authors listed] A Philippidis - Human Gene Therapy, 2021 - liebertpub.com GSID: F26j86SuKiYJ
The platform vector gene therapies project: Increasing the efficiency of adeno-associated virus gene therapy clinical trial startup. Lomash RM. PJ Brooks, EA Ottinger, D Portero, RM Lomash… - Human Gene …, 2020 - liebertpub.com GSID: klfhDiltzgIJ
Quality control testing, characterization and critical quality attributes of adeno‐associated virus vectors used for human gene therapy. Wright JF. JF Wright - Biotechnology Journal, 2021 - Wiley Online Library GSID: 6z4TAxb_NlIJ
Directed evolution of a family of AAV capsid variants enabling potent muscle-directed gene delivery across species. King EM, Lagerborg KA, Stanton A, Tabebordbar M. M Tabebordbar, KA Lagerborg, A Stanton, EM King… - Cell, 2021 - Elsevier GSID: CF8E1WX4IM4J
