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Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors.

Molecular therapy. Methods & clinical development

Dias Florencio G, Precigout G, Beley C, Buclez PO, Garcia L, Benchaouir R.
PMID: 26207258
Mol Ther Methods Clin Dev. 2015 Jul 15;2:15024. doi: 10.1038/mtm.2015.24. eCollection 2015.

Recombinant adeno-associated viruses (rAAV) are promising candidates for gene therapy approaches. The last two decades were particularly fruitful in terms of processes applied in the production and purification of this type of gene transfer vectors. This rapid technological evolution...

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Dias Florencio G, Precigout G, Beley C, et al. Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors. Mol Ther Methods Clin Dev. 2015;2:15024doi: 10.1038/mtm.2015.24.
Dias Florencio, G., Precigout, G., Beley, C., Buclez, P. O., Garcia, L., & Benchaouir, R. (2015). Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors. Molecular therapy. Methods & clinical development, 215024. https://doi.org/10.1038/mtm.2015.24
Dias Florencio, Gabriella, et al. "Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors." Molecular therapy. Methods & clinical development vol. 2 (2015): 15024. doi: https://doi.org/10.1038/mtm.2015.24
Dias Florencio G, Precigout G, Beley C, Buclez PO, Garcia L, Benchaouir R. Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors. Mol Ther Methods Clin Dev. 2015 Jul 15;2:15024. doi: 10.1038/mtm.2015.24. eCollection 2015. PMID: 26207258; PMCID: PMC4502676.
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Rapid, scalable, and low-cost purification of recombinant adeno-associated virus produced by baculovirus expression vector system.

Molecular therapy. Methods & clinical development

Buclez PO, Dias Florencio G, Relizani K, Beley C, Garcia L, Benchaouir R.
PMID: 27226971
Mol Ther Methods Clin Dev. 2016 May 11;3:16035. doi: 10.1038/mtm.2016.35. eCollection 2016.

Recombinant adeno-associated viruses (rAAV) are largely used for gene transfer in research, preclinical developments, and clinical trials. Their broad in vivo biodistribution and long-term efficacy in postmitotic tissues make them good candidates for numerous gene transfer applications. Upstream processes...

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Buclez PO, Dias Florencio G, Relizani K, et al. Rapid, scalable, and low-cost purification of recombinant adeno-associated virus produced by baculovirus expression vector system. Mol Ther Methods Clin Dev. 2016;3:16035doi: 10.1038/mtm.2016.35.
Buclez, P. O., Dias Florencio, G., Relizani, K., Beley, C., Garcia, L., & Benchaouir, R. (2016). Rapid, scalable, and low-cost purification of recombinant adeno-associated virus produced by baculovirus expression vector system. Molecular therapy. Methods & clinical development, 316035. https://doi.org/10.1038/mtm.2016.35
Buclez, Pierre-Olivier, et al. "Rapid, scalable, and low-cost purification of recombinant adeno-associated virus produced by baculovirus expression vector system." Molecular therapy. Methods & clinical development vol. 3 (2016): 16035. doi: https://doi.org/10.1038/mtm.2016.35
Buclez PO, Dias Florencio G, Relizani K, Beley C, Garcia L, Benchaouir R. Rapid, scalable, and low-cost purification of recombinant adeno-associated virus produced by baculovirus expression vector system. Mol Ther Methods Clin Dev. 2016 May 11;3:16035. doi: 10.1038/mtm.2016.35. eCollection 2016. PMID: 27226971; PMCID: PMC4867670.
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Exon Skipping in a Dysf-Missense Mutant Mouse Model.

Molecular therapy. Nucleic acids

Malcher J, Heidt L, Goyenvalle A, Escobar H, Marg A, Beley C, Benchaouir R, Bader M, Spuler S, García L, Schöwel V.
PMID: 30292141
Mol Ther Nucleic Acids. 2018 Dec 07;13:198-207. doi: 10.1016/j.omtn.2018.08.013. Epub 2018 Aug 22.

Limb girdle muscular dystrophy 2B (LGMD2B) is without treatment and caused by mutations in the dysferlin gene (DYSF). One-third is missense mutations leading to dysferlin aggregation and amyloid formation, in addition to defects in sarcolemmal repair and progressive muscle...

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Malcher J, Heidt L, Goyenvalle A, et al. Exon Skipping in a Dysf-Missense Mutant Mouse Model. Mol Ther Nucleic Acids. 2018;13:198-207doi: 10.1016/j.omtn.2018.08.013.
Malcher, J., Heidt, L., Goyenvalle, A., Escobar, H., Marg, A., Beley, C., Benchaouir, R., Bader, M., Spuler, S., García, L., & Schöwel, V. (2018). Exon Skipping in a Dysf-Missense Mutant Mouse Model. Molecular therapy. Nucleic acids, 13198-207. https://doi.org/10.1016/j.omtn.2018.08.013
Malcher, Jakub, et al. "Exon Skipping in a Dysf-Missense Mutant Mouse Model." Molecular therapy. Nucleic acids vol. 13 (2018): 198-207. doi: https://doi.org/10.1016/j.omtn.2018.08.013
Malcher J, Heidt L, Goyenvalle A, Escobar H, Marg A, Beley C, Benchaouir R, Bader M, Spuler S, García L, Schöwel V. Exon Skipping in a Dysf-Missense Mutant Mouse Model. Mol Ther Nucleic Acids. 2018 Dec 07;13:198-207. doi: 10.1016/j.omtn.2018.08.013. Epub 2018 Aug 22. PMID: 30292141; PMCID: PMC6172476.
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Showing 1 to 3 of 3 entries